Orphan Drugs As A Lifeline for Rare Diseases

Nadiah Hanim Abdul Latif, President, Malaysia Rare Disorders Society | Professor Dr Thong Meow Keong, Consultant Paediatrician & Clinical Geneticist

15-Jan-25 16:00

Orphan Drugs As A Lifeline for Rare Diseases

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When speaking to individuals with rare disorders or their families, it’s not uncommon to hear about the diagnostic odyssey they’ve been through just to get a name for what they’re going through. But what happens after that? We want to look beyond the diagnosis, to understand what are the challenges they still face. Today, we’ll be exploring what access to medicines looks like for rare disorders and the importance of orphan drugs to these individuals and their families.

Image credit: Shutterstock

Produced by: Lim Sue Ann

Presented by: Lim Sue Ann

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Categories: managing disease, wellness, health policy

Tags: the bigger picture, health and living, rare disease, orphan drugs, genetic diseases,

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