Orphan Drugs As A Lifeline for Rare Diseases

Nadiah Hanim Abdul Latif, President, Malaysia Rare Disorders Society | Professor Dr Thong Meow Keong, Consultant Paediatrician & Clinical Geneticist

15-Jan-25 16:00

Orphan Drugs As A Lifeline for Rare Diseases

Pause
Embed

When speaking to individuals with rare disorders or their families, it’s not uncommon to hear about the diagnostic odyssey they’ve been through just to get a name for what they’re going through. But what happens after that? We want to look beyond the diagnosis, to understand what are the challenges they still face. Today, we’ll be exploring what access to medicines looks like for rare disorders and the importance of orphan drugs to these individuals and their families.

Image credit: Shutterstock

Produced by: Lim Sue Ann

Presented by: Lim Sue Ann

This and more than 60,000 other podcasts in your hand. Download the all new BFM mobile app.

Categories: managing disease, wellness, health policy

Tags: the bigger picture, health and living, rare disease, orphan drugs, genetic diseases,

Today’s Shows

11:00 AM

Best of Enterprise

(REPEAT) Dr. Carmelo Ferlito, CEO of the Center for Market Education, joins us to break down the flawed logic behind the U.S. tariff calculations, the broader risks of a global trade war, and what Malaysian businesses and policymakers should do in response.

12:00 PM

Just For Kicks

(REPEAT) Kam and his pundits break down the midweek European action, as well as look ahead to Matchweek 32 of the EPL.

1:00 PM

A Bit of Culture

(REPEAT) Kam and his trusted sidekicks, Dhanya Nair and Julian Yap get together again to talk about what Kam has learned after publishing his new book, how do you know you’re an adult and the joy of missing out!

2:00 PM

Ringgit & Sense

(REPEAT) Ringgit and Sense producer Jake Lim speaks to Jennifer Chua, licensed Financial Advisor at UOB Kay Hian to discuss what’s involved in planning for your parents’ aged care.

2:30 PM

The Property Show

(REPEAT) Siva Shanker, the CEO of Real Estate Agency of Rahim & Co International takes us through his observations of 2024, the first quarter of 2025 and how the rest of this year might shape up in the property world.

3:00 PM

Best of The Bigger Picture

(REPEAT) Professor Jomo Kwame Sundaram breaks down the effect of Trump’s tariffs on neoliberalism and the dollar dominance.

4:00 PM

Best of Evening Edition

(REPEAT) Malaysian poet Jack Malik talks about the evolution of Malaysian poetry and how our multilingualism and rich cultural history shape the art form.

5:00 PM

BBC World Service

BFM presents the BBC World Service, which provides in-depth coverage of issues from around the world.

PROGRAMMES